Purpose

Three-day intensive small group workshop trains participants to confidently advance drug development and research goals for their communities. Focused on the development of Central Nervous System (CNS)–based therapies and designed for rare disease patient advocates who are already funding or directly engaging in research. The program blends expert-led learning with practical skill-building in areas including brain structure and function, in vivo and in vitro research tools, diagnostics, therapeutic modalities, IND-enabling studies, clinical research, and regulatory pathways. 

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Impact

• Direct interaction with thought leaders - including CEOs of some of the most innovative therapeutic development companies, along with experts pioneering legal and regulatory practices.

• Unparalleled insights into the cutting edge of drug development and regulatory science

• Open pathways for lasting partnerships